Global Genes® - 2024 NEXT Report

Global Genes® NEXT Report 2024: Rewriting the Rules. Despite facing financial challenges, the rare disease sector has made remarkable strides with a notable surge in the approval of new medications. Patient advocates in the rare disease community have been instrumental in driving research and drug development by collecting vital data, supporting crucial research, and taking on projects that companies may have hesitated to pursue. Their unwavering determination and sense of urgency are reshaping the boundaries of what is achievable. The 2024 NEXT Report highlights these accomplishments in conjunction with the ever-evolving landscape of innovation and technology, revolutionizing the speed of diagnosing and treating rare diseases.